Optimizing In Vivo Delivery & Dosing Strategies to Maximize mRNA Therapeutic Efficacy & Safety

2:00 pm - Wednesday 28th January 2026

  • Comparing systemic vs local delivery strategies for achieving tissue-specific expression
  • Examining how lipid type, ionizable components, and dosing schedule impact safety and immunogenicity
  • Reviewing preclinical to clinical case studies where formulation or dosing adjustments significantly impacted trial outcomes

Speakers:

Chief Executive Officer & Head of Translational Research & Alliance Management
Pantherna Therapeutics