Exploring Novel Tools for Intracellular Delivery of RNA Therapeutics: From Small Molecules to Proteins

Time: 2:30 pm
day: Focus Day


  • Repurposing of cationic amphiphilic drugs (CADs) to promote cytosolic delivery of small nucleic acid therapeutics (siRNAs, ASOs)
  • Exploiting CADs as structural and functional components of lipid nanoparticles (LNPs) for cytosolic delivery of mRNA
  • Applying lung surfactant proteins as endogenous and biocompatible enhancers of intracellular RNA delivery